Status | Study |
Enrolling by invitation |
Study Name: Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA Condition: Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) Date: 2013-07-24 Interventions: Drug: scAAVrh74.tMCK.hSGCA |
Recruiting |
Study Name: Limb Girdle Muscular Dystrophy (LGMD) Natural History Condition: Muscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED) Date: 2013-01-18 |
Active, not recruiting |
Study Name: Clinical Outcome Study for Dysferlinopathy Condition: Dysferlinopathy LGMD2B Miyoshi Myopathy Date: 2012-08-28 |
Completed |
Study Name: Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C Condition: Limb Girdle Muscular Dystrophy Type 2C Gamma-sarcoglycanopathy Date: 2011-03-17 Interventions: Biological: AAV1-gamma-sarcoglycan vector injection single intramuscular injection into carpi radialis m |
Enrolling by invitation |
Study Name: Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies Condition: Duchenne Muscular Dystrophy Becker Muscular Dystrophy Date: 2010-05-18 Interventions: Drug: Coenzyme Q10 and Lisinopril Arm 1. Coenzyme Q10: taken once a day each morning by mouth OR Arm 2. |
Completed |
Study Name: Cardiac Magnetic Resonance in Children With Muscular Dystrophy Condition: Duchenne Muscular Dystrophy Becker Muscular Dystrophy Date: 2010-03-04 |
Completed |
Study Name: Cardiac Outcome Measures in Children With Muscular Dystrophy Condition: Duchenne Muscular Dystrophy Becker Muscular Dystrophy Date: 2010-02-09 |
Completed |
Study Name: Evaluation of Limb-Girdle Muscular Dystrophy Condition: Becker Muscular Dystrophy Limb-Girdle Muscular Dystrophy, Type Date: 2009-05-04 |
Completed |
Study Name: Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy Condition: Muscular Dystrophies Duchenne Muscular Dystrophy Becker Mu Date: 2009-04-01 Interventions: Other: Retrograde high pressure transvenous perfusion with normal saline Dose escalation of saline volum |
Completed |
Study Name: Deflazacort in Dysferlinopathies Condition: LGMD2B Miyoshi Myopathy Dysferlinopathy Date: 2007-09-06 Interventions: Drug: deflazacort In the first |